Buscar resultados de ensayos clínicos
Lysosomal Storage Diseases, Nervous System - 25 Studies Found
Estado | Estudiar |
Recruiting |
Nombre del estudio: Long-term Outcome in Late-onset Pompe Disease Treated Beyond 36 Months (ATBIG-Pompe-Study) Condición: Pompe Disease Fecha: 2016-06-20 Intervenciones: Drug: glucosidase alfa Long-term use in an observational study of licenced drug |
Recruiting |
Nombre del estudio: Respiratory Muscle Training in L-Onset Pompe Disease (LOPD) Condición: Glycogen Storage Disease Type II Fecha: 2016-06-13 Intervenciones:
|
Recruiting |
Nombre del estudio: Study to Compare the Efficacy and Safety of Enzyme Replacement Therapies neoGAA and Alglucosidase Alfa Administered Every Other Week in Patients With Late-onset Pompe Disease Who Have Not Been Previously Treated for Pompe Disease Condición: Glycogen Storage Disease Type II-Pompe's Disease Fecha: 2016-05-23 Intervenciones:
|
Recruiting |
Nombre del estudio: Identification of Tongue Involvement in Late-Onset Pompe Disease Condición:
|
Recruiting |
Nombre del estudio: Pompe Disease QMUS and EIM Condición: Pompe Disease Fecha: 2016-04-11 Intervenciones:
|
Enrolling by invitation |
Nombre del estudio: An MRI Study on Muscular Diseases -Pompe Disease and Dystrophia Myotonica- Condición:
Fecha: 2015-12-08 |
Active, not recruiting |
Nombre del estudio: First-In-Human Study to Evaluate Safety, Tolerability, and PK of Intravenous ATB200 Alone and When Co-Administered With Oral AT2221 Condición: Pompe Disease Fecha: 2016-01-26 Intervenciones:
|
Recruiting |
Nombre del estudio: Safety and Effectiveness of Resistance Exercise Training in Patients With Pompe Disease. Condición:
Fecha: 2015-12-10 Intervenciones: Other: Resistance Exercise Training Resistance Exercise Tr |
Not yet recruiting |
Nombre del estudio: Prevalence of Pompe's Disease in Respiratory Clinics Condición: Pompe's Disease Fecha: 2015-08-17 Intervenciones: Other: Prospective observational study Prospective observational study collecting data during a clinic v |
Recruiting |
Nombre del estudio: Immune Modulation Therapy for Pompe Disease Condición: Pompe Disease Fecha: 2015-08-10 Intervenciones:
|